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2024
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G/S
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Pharmaceutical preparations, namely, for the activation of PKR (pyruvate kinase R), for the activ... |
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Invention
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Mitapivat therapy and modulators of cytochrome p450.
Described herein are methods of treating py... |
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Invention
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4-pyrazolo[1,5-a]pyridin-2-yl-4,5,6,7-tetrahydro-1 h-imidazo[4,5-c]pyridine derivatives as mutant... |
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Invention
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Compounds and methods useful for stabilizing phenylalanine hydroxylase mutations.
The disclosure... |
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Invention
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4-pyrazolo[1,5-a]pyridin-2-yl-4,5,6,7-tetrahydro-1h-imidazo[4,5-c]pyridine derivatives as mutant ... |
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Invention
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Synthesis of pyruvate kinase activators. Provided herein are methods for preparing activators of ... |
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Invention
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Bcat2 inhibitors. The disclosure is directed to compounds, and pharmaceutically acceptable salts ... |
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Invention
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Crystalline salts or amorphous forms of 2-((1h-pyrazol-3-yl)methyl)-6-((6-aminopyridin-2-yl)methy... |
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G/S
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Education services, namely, providing mentoring, tutoring, classes, seminars and workshops in the... |
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G/S
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Promoting public awareness of hematological disorders and their treatment and management Educatio... |
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G/S
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downloadable software in the nature of a mobile application to allow patients and healthcare prof... |
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G/S
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Pharmaceutical preparations for the prevention and treatment
of genetically defined diseases, he... |
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G/S
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Pharmaceutical preparations, namely, for the activation of
PKR (pyruvate kinase R), for the acti... |
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2023
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Invention
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Therapeutic compounds and compositions.
Compounds and compositions comprising compounds that mod... |
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Invention
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Porphyria disease models. Described herein are mouse models of porphyrias, including mouse models... |
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Invention
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Pyruvate kinase activators for use in therapy.
Described herein are methods for using compounds ... |
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Invention
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Compounds and methods useful for stabilizing phenylalanine hydroxylase mutations. 5A, and L are d... |
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G/S
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Downloadable electronic publications in the nature of posters, manuscripts, abstracts and white p... |
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Invention
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(4-benzo[d]oxazol-2-yl)-6,7-dihydro-1h-imidazo[4,5-c]pyridine-5(4h)-yl)methanone derivatives as m... |
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Invention
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Compounds and methods useful for stabilizing phenylalanine hydroxylase mutations. The disclosure ... |
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Invention
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Compounds and methods useful for stabilizing phenylalanine hydroxylase mutations |
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Invention
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Pyruvate kinase activators for use in treating blood disorders. k, and Q are as defined herein.
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2022
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Invention
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Compounds for treating mds-associated anemias and other conditions.
Provided herein is the use o... |
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Invention
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Compounds for treating mds-associated anemias and other conditions. Provided herein is the use of... |
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Invention
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Pyruvate kinase activators for use in treating blood disorders. 2 are as defined herein.
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Invention
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Methods for titrating mitapivat.
Provided herein are safe and effective dosing regimens for mita... |
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G/S
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Downloadable podcasts in the fields of medicine, science, medical patient care, and medical diagn... |
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Invention
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Methods for titrating mitapivat. Provided herein are safe and effective dosing regimens for mitap... |
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Invention
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Pyruvate kinase modulators and use thereof. Described herein are methods of using compounds of Fo... |
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Invention
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Crystalline forms of n-(4-(4-(cyclopropylmethyl)piperazine-1-carbonyl)phenyl)quinoline-8-sulfonam... |
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2021
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Invention
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Methods of using pyruvate kinase activators.
Described herein are methods for using compounds th... |
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G/S
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Pharmaceutical preparations for the prevention and treatment of genetically defined diseases, hem... |
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G/S
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Providing medical and scientific research information in the field of clinical trials Providing h... |
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Invention
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Pharmaceutical formulation.
Disclosed is a pharmaceutical mini-tablet comprising mitapivat or a ... |
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Invention
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Pharmaceutical formulation. Disclosed is a pharmaceutical mini-tablet comprising mitapivat or a p... |
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Invention
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Automated identification of potential drug safety events.
Various embodiments include methods, c... |
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G/S
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Specimen collection kits for use in genetic testing comprised primarily of sample collection cont... |
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G/S
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Specimen collection kits for use in genetic testing comprised primarily of saliva and blood colle... |
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Invention
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Methods for titrating mitapivat for use in treating thalassemia. Provided herein are safe and eff... |
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Invention
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Menin inhibitors and methods of use for treating cancer. The present disclosure provides compound... |
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Invention
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Pyruvate kinase activators for use in therapy. Described herein are methods for using compounds t... |
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Invention
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Methods of treating autoimmune or inflammatory diseases or disorders. The disclosure is directed ... |
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2020
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Invention
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Therapeutic compounds and compositions. Compounds and compositions comprising compounds that modu... |
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Invention
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Deuterated analogs of an idh1 inhibitor. Provided are deuterated analogs of a compound and method... |
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Invention
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Piperidine compounds as menin inhibitors. The present disclosure provides compounds represented b... |
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Invention
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Mitapivat therapy and modulators of cytochrome p450. Described herein are methods of treating pyr... |
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Invention
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Methods of treatment with aminolevulinic acid synthase 2 (alas2) modulators.
Described herein is... |
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Invention
|
Crystalline salt forms of n-(4-(4-(cyclopropylmethyl)piperazine-1-carbonyl)phenyl)quinoline-8-sul... |
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Invention
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Thieno[3,2-b] pyrrole[3,2-d]pyridazinone derivatives and their use as pkm2 derivatives for the tr... |
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G/S
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Pharmaceutical products for the prevention and treatment of
blood disorders; pharmaceutical prod... |
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G/S
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Pharmaceutical products for the prevention and treatment of blood disorders; pharmaceutical produ... |
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2018
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G/S
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Patient support services to help eligible patients obtain access to or afford prescription drugs ... |
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2017
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G/S
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Anti-cancer preparations, pharmaceutical products for the
prevention and treatment of cancer, bi... |
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G/S
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Anti-cancer preparations, pharmaceutical products for the prevention and treatment of cancer, bio... |
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G/S
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Anti-cancer preparations; pharmaceutical products for the prevention and treatment of cancer; bio... |
