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2025
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P/S
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Downloadable electronic publications in the nature of books, manuals, booklets, pamphlets and bro... |
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P/S
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Pharmaceutical preparations for the treatment of genetic diseases and disorders. |
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2024
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P/S
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Providing online, non-downloadable software using artificial intelligence (AI) in the biopharmace... |
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P/S
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Providing online, non-downloadable software using artificial
intelligence (AI) in the biopharmac... |
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P/S
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Biotechnology research; chemical engineering; providing
information on scientific and research s... |
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P/S
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Biotechnology research; chemical engineering; providing information on scientific and research st... |
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P/S
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Biotechnology research; Chemical engineering; Providing information on scientific and research st... |
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P/S
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Pharmaceutical preparations for the treatment of genetic diseases and disorders |
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Invention
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Methods for increasing vatiquinone plasma exposure with food. The present disclosure relates to v... |
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Invention
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Carboline compounds and use thereof. [0536] Provided herein are p-carboline compounds of Formula ... |
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Invention
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Crystalline forms of 2-[3-(2,2,6,6-tetramethylpiperidin-4-yl)-3h-[1,2,3]triazolo[4,5-c]pyridazin-... |
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Invention
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Novel rna transcript.
An alternatively spliced intronic sequence is disclosed, the splicing of w... |
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P/S
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Pharmaceutical preparations for the treatment of genetic disorders |
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2023
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Invention
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Heterocyclic and heteroaryl compounds as inhibitors of nlrp3. The present invention relates to no... |
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P/S
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Pharmaceutical preparations for the treatment of genetic diseases and disorders. |
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P/S
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Pharmaceutical preparations for the treatment of genetic
diseases and disorders. |
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Invention
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Heterocyclic and heteroaryl compounds for treating huntington's disease.
Disclosed are quinoline... |
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Invention
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Oxidative cleavage method of trolox amide. The present disclosure provides an oxidative cleavage ... |
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Invention
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Granules for suspension. The present disclosure provides granules for suspension. Specifically, t... |
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Invention
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Methods of producing 2,3,5,6-alkyl-1,4-benzoquinones. The application discloses methods useful fo... |
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Invention
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Pharmaceutical compositions comprising 2,3,5-trimethyl-6-nonylcyclohexa-2,5-diene-1,4-dione.
Dis... |
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Invention
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Polymorphs of sepiapterin and salts thereof. Disclosed are crystalline forms of sepiapterin free ... |
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Invention
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Pharmaceutical compositions comprising sepiapterin and uses thereof. The present invention featur... |
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Invention
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Methods for modulating rna splicing. A method for modulating an amount or type of a mature RNA tr... |
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Invention
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Compounds for treating spinal muscular atrophy.
Provided herein are compounds of Formula (I):
... |
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P/S
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Downloadable electronic publications in the nature of Spanish language books, manuals, booklets, ... |
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Invention
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Polymorphic forms of (r)-2-hydroxy-2-methyl-4-(2,4,5-trimethyl-3,6-dioxocyclohexa-1,4-dienyl)buta... |
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Invention
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2,3,5-trimethyl-6-nonylcyclohexa-2,5-diene-1,4-dione for suppressing and treating alpha-synuclein... |
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Invention
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Compounds for treating spinocerebellar ataxia type 3 |
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Invention
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Compounds for treating spinocerebellar ataxia type 3. An aspect of the present description relate... |
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Invention
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Compounds for treating huntington's disease.
The present description relates to compounds, forms... |
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Invention
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Heterocyclic and heteroaryl compounds for treating huntington's disease. The present description ... |
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P/S
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Pharmaceutical preparations for treating genetic diseases and disorders; pharmaceutical preparati... |
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Invention
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Methods for modulating rna splicing.
In one aspect, described herein is an intronic recognition ... |
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Invention
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Methods for increasing sepiapterin plasma exposure.
The present invention features compositions ... |
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Invention
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Methods for treating cancer and non-neoplastic conditions.
Compounds that selectively inhibit pa... |
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Invention
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Gene therapy of ush2a-associated diseases. The disclosure describes the discovery of a dual targe... |
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Invention
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Methods for treating huntington’s disease.
The present description relates to compounds, forms, ... |
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Invention
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Inhibitors of nlrp3. The present invention relates to compounds that are useful as inhibitors of ... |
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Invention
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Methods for modulating rna splicing.
In one aspect, described herein is a recognition element fo... |
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2022
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Invention
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Carboline compounds and use thereof. Provided herein are ?-carboline compounds and their use to i... |
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Invention
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Carboline compounds and use thereof. Provided herein are β-carboline compounds and their use to i... |
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Invention
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Compositions for an orally active 1,2,4-oxadiazole for the treatment of disease.
The present inv... |
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Invention
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Pharmaceutical composition of sepiapterin.
This invention discloses a pharmaceutical composition... |
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Invention
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Pharmaceutical composition of sepiapterin. This invention discloses a pharmaceutical composition ... |
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Invention
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Methods of producing 2, 3, 5, 6-alkyl-1, 4-benzoquinones. The application discloses methods usefu... |
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Invention
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Methods for treating neurogenerative diseases.
The present description relates to methods of tre... |
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Invention
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Heteroaryl compounds for treating huntington's disease.
The present description relates to compo... |
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Invention
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Methods for synthesis of racemic, scalemic, and chiral alpha-tocotrienol quinone.
The applicatio... |
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Invention
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2-substituted amino-naphth (1,2-d) imidazol-5-one compounds of pharmaceutically acceptable salts ... |
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Invention
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Methods for treating covid-19 with sepiapterin.
The invention features methods of treating a SAR... |
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Invention
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Methods for treating glioblastomas with sepiapterin.
The invention features methods of treating ... |
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Invention
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Methods for treating spinocerebellar ataxia type 3.
The present description relates to methods o... |
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2021
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Invention
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Tablet for use in treating huntington's disease and method of making the same.
The present descr... |
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Invention
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Dhodh inhibitor for the treatment of covid-19.
One aspect described herein includes a method for... |
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Invention
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Compounds for treating huntington's disease.
The present description relates to compounds of For... |
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Invention
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Methods for treating parkinson's disease with sepiapterin.
The present invention features method... |
