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2025
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Invention
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Utilization of infant activated audio player.
One aspect of the present disclosure include a met... |
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Invention
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Treatment of spinal muscular atrophy by inducing heat shock response.
A method of treating spina... |
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Invention
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Products and methods for treating diseases or disorders associated with dux4 overexpression. Disc... |
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Invention
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Splice-switching oligonucleotides targeting insulin receptor as a cancer therapeutic. The disclos... |
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Invention
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Self-complementary adeno-associated virus vector and its use in treatment of muscular dystrophy. ... |
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Invention
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Products and methods for inhibition of expression of dynamin-1 variants.
RNA interference-based ... |
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Invention
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Gene therapy for treating gne-related disorders. The present invention relates to methods and mat... |
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Invention
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Products and methods to inhibit expression of dynamin-1 variants and replace dynamin-1. [215] RNA... |
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Invention
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Crispr/cas9 based treatment for protein mutations associated with multisystem proteinopathy. The ... |
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Invention
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Exon 17-targeted nucleic acids, compositions, and methods for treatment of dystrophin-based myopa... |
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Invention
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Methods of increasing nk cell efficacy through inhibition of v-domain ig suppressor of t cell act... |
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Invention
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Products and methods for treatment of amyotrophic lateral sclerosis.
The present invention relat... |
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2024
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Invention
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Adeno-associated virus vector delivery of alpha-sarcoglycan and the treatment of muscular dystrop... |
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Invention
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Antibody compositions for disrupting biofilms.
Provided herein are methods and compositions for ... |
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Invention
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Anticoagulants for treating nephrotic syndrome. A method of treating or preventing glomerular dis... |
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Invention
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Compositions and methods of making a modified gamma-delta t-cell. Disclosed herein is a method of... |
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Invention
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Compositions and methods for treating diseases or conditions associated with progerin expression.... |
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Invention
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Tracheostomy trainer and method of use. A tracheostomy trainer includes a head pivotally connecte... |
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Invention
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Adeno-associated virus vector delivery of micro-dystrophin to treat muscular dystrophy.
The inve... |
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Invention
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Methods and materials for galgt2 gene therapy.
The present disclosure relates to recombinant ade... |
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Invention
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Systems and methods for optimized patient specific tissue engineering vascular grafts.
It has be... |
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Invention
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Methods for determining antibiotic sensitivity.
Disclosed are approaches to determining a sensit... |
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Invention
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Brace compliance system and method of use. A brace compliance system and method of use are descri... |
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Invention
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Audio device and method of use.
A sanitizable audio device for use in neonatal care and method o... |
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Invention
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Methods of quantifying skeletal muscle perfusion using pet imaging.
Described herein are methods... |
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Invention
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Novel cell-free mirna biomarkers in maternal blood for detection of single ventricle defects in f... |
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Invention
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Mutation repair methods and related compositions. Disclosed herein are systems for repairing or c... |
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Invention
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Materials and methods for the treatment of neurofibromin 1 mutations and diseases resulting there... |
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Invention
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Gene therapy for lysosomal acid lipase deficiency (lal-d). The disclosure provides gene therapy v... |
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Invention
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Assays and methods for quality control of genome packaging for gene therapy. The present disclosu... |
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Invention
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Grna for targeting mutant allele and uses thereof. Disclosed herein are systems for modulating mu... |
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Invention
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Cd-33 protein-binding compositions and methods related thereto. Disclosed are single-chain variab... |
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Invention
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Systems and methods for predicting cardiac risk of anomalous aortic origin of coronary artery. A ... |
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Invention
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Protein engineering micro-tuberin gene therapy candidates for tuberous sclerosis complex type 2. ... |
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Invention
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A modular system to convert therapeutic microrna expression cassettes from polymerase iii-based t... |
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Invention
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Gene therapy for treatment of protein misfolding diseases. Provided are gene therapy vectors, suc... |
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Invention
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Treatment of multiple sclerosis using nt-3 gene therapy. The present disclosure relates to method... |
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Invention
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Methods and materials for nt-3 gene therapy.
The present disclosure relates to recombinant adeno... |
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Invention
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Modified u6 promoter system for tissue specific expression.
The present invention relates to a t... |
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2023
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Invention
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Il-27 expressing oncolytic viruses.
A recombinant interleukin-27 (IL27) expressing virus is desc... |
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Invention
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Method of gene targeting utilizing outer membrane vesicle.
A method of gene targeting utilizing ... |
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Invention
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Materials and methods for the treatment of eif2b5 mutations and diseases resulting therefrom.
Pr... |
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Invention
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Bacterial biofilm inhibitors.
Compounds according to formula I: wherein Ar is an aryl or heteroa... |
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2022
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Invention
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Materials and methods for the treatment of limb girdle muscular dystrophy.
Provided are gene the... |
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Invention
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Chimeric hsv expressing hil21 to boost anti-tumor immune activity.
Provided herein are non-natur... |
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Invention
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Materials and methods for slc6a1 gene therapy.
The present disclosure relates to methods of trea... |
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Invention
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Neuregulin for protection against respiratory viral infection and post-viral disease.
A method o... |
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Invention
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Products and methods for myelin protein zero silencing and treating cmt1b disease.
RNA interfere... |
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Invention
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Enhanced cell-derived vesicles for cancer therapy.
This disclosure relates to populations and co... |
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Invention
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Methods of treating nephrotic syndrome.
A method of treating nephrotic syndrome (NS) in a subjec... |
