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2024
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G/S
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Pharmaceutical preparations for the treatment of cystic fibrosis. |
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G/S
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Pharmaceutical preparations for the treatment of cystic
fibrosis. |
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G/S
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Pharmaceutical preparations for the treatment of cystic fibrosis |
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Invention
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Precise excisions of portions of exons for treatment of duchenne muscular dystrophy.
Composition... |
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Invention
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Differentiation of pancreatic endocrine cells.
Disclosed herein are compositions and methods rel... |
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Invention
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Affinity purification methods for adeno associated viruses (aavs). Provided herein are isolated p... |
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Invention
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Methods for directing lipid nanoparticles in vivo. Compositions and methods for enhancing payload... |
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Invention
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Compact proteins. Disclosed herein are compositions of compact proteins such as compact nucleobas... |
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Invention
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Stem cell derived pancreatic islet differentiation.
Disclosed herein are compositions and method... |
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G/S
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Providing health information to patients and caregivers; providing health care information; provi... |
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Invention
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Hypoimmune cells.
Disclosed herein are compositions and methods related to isolated cells (e.g.,... |
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G/S
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Educational services, namely, providing classes, seminars, and workshops in the fields of medicat... |
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Invention
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Materials and methods for treatment of hemoglobinopathies.
Materials and methods for treating a ... |
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Invention
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Precise excisions of portions of exon 51 for treatment of duchenne muscular dystrophy.
Compositi... |
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Invention
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Islet cell manufacturing compositions and methods of use.
Disclosed herein are compositions and ... |
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Invention
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Macroencapsulation devices including immunomodulatory compounds. Macroencapsulation devices and t... |
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Invention
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Gene editing of regulatory elements.
Compositions and methods for disrupting and/or excising reg... |
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Invention
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Biaryl amide-containing agonists of orexin receptor type 2. Disclosed are compounds, compositions... |
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G/S
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Pharmaceuticals and medicines for the treatment of cystic fibrosis, pain, sickle cell disease, be... |
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G/S
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Pharmaceuticals and medicines for the treatment of cystic
fibrosis, pain, sickle cell disease, b... |
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2023
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Invention
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Re-aggregation of stem cell-derived pancreatic beta cells.
The present application discloses cel... |
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Invention
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Differentiation of pancreatic endocrine cells. Disclosed herein are compositions and methods rela... |
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G/S
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Pharmaceuticals and medical treatment products in the field of diabetes; cell therapy products fo... |
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G/S
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Pharmaceuticals and medical treatments in the field of diabetes; cell therapy products for medica... |
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G/S
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Pharmaceuticals and medical treatments in the field of
diabetes; cell therapy products for medic... |
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G/S
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Pharmaceuticals and medical treatment products in the field
of diabetes; cell therapy products f... |
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G/S
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Pharmaceutical preparations for treating diabetes; medical treatments in the nature of anti-diabe... |
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G/S
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Pharmaceutical preparations for treating diabetes; medical
treatments in the nature of anti-diab... |
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Invention
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Process for the synthesis of substituted tetrahydrofuran modulators of sodium channels. Provided ... |
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Invention
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Substituted tetrahydrofurans as modulators of sodium channels.
Compounds, and pharmaceutically a... |
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Invention
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Substituted macrocyclic amine modulators of orexin receptor 2. Disclosed are compounds, compositi... |
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Invention
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Inhibitors of apol1 and methods of using same.
The disclosure provides at least one entity chose... |
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Invention
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Genetically engineered cells. Disclosed herein are compositions and methods related to geneticall... |
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Invention
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N-(hydroxyalkyl (hetero)aryl) tetrahydrofuran carboxamides as modulators of sodium channels.
Com... |
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Invention
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Modulators of alpha-1 antitrypsin.
The disclosure provides compounds useful for treating alpha-1... |
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Invention
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Modulators of cystic fibrosis transmembrane conductance regulator, pharmaceutical compositions, m... |
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Invention
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Methods of treating apol-1 dependent focal segmental glomerulosclerosis.
This application descri... |
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G/S
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medical and scientific research; medical and scientific research in the field of gene therapy; me... |
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Invention
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Cell housing device.
The present disclosure provides a cell housing device and a method of manuf... |
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Invention
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Enhanced differentiation of pancreatic islet cells. Disclosed herein are compositions and methods... |
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Invention
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Materials and methods for treatment of pain related disorders.
The present application provides ... |
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Invention
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Modulators of alpha-1 antitrypsin.
Novel compounds, compositions, and methods of using and prepa... |
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Invention
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Modulators of alpha-1 antitrypsin. Novel compounds, compositions, and methods of using and prepar... |
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Invention
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Compositions and methods for treatment of myotonic dystrophy type 1 with crispr/sacas9.
Composit... |
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Invention
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Compositions and methods for treatment of myotonic dystrophy type 1 with crispr/slucas9.
Composi... |
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G/S
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Providing on-line non-downloadable software for use by healthcare professionals to view and acces... |
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G/S
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Providing health information in the field of sickle cell disease; providing health care informati... |
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Invention
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Compositions for the treatment of cftr-mediated diseases. RNN-[2,4-Bis(1,1-dimethylethyl)-5-hydro... |
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G/S
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Providing information in the field of gene editing technology; Providing medical and scientific r... |
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Invention
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Pharmaceutical composition and administrations thereof.
The present invention relates to pharmac... |
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Invention
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Tandem guide rnas (tg-rnas) and their use in genome editing. Compositions comprising tandem gRNAs... |
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Invention
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Factor b proteases.
Provided herein are engineered proteases of the S1A family that are specific... |
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Invention
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Processes for making modulators of cystic fibrosis transmembrane conductance regulator. The discl... |
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G/S
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Providing online non-downloadable software featuring a
portal for order management and maintaini... |
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G/S
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Educational services, namely, providing classes, seminars,
and workshops in the fields of medica... |
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G/S
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Providing online non-downloadable software featuring a portal for order management and maintainin... |
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Invention
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Modulators of atp-binding cassette transporters.
Compounds of the present invention and pharmace... |
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2022
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Invention
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Stem cell differentiation and chemical compounds.
Disclosed herein are compositions and methods ... |
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Invention
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Processes for making modulators of cystic fibrosis transmembrane conductance regulator.
The disc... |
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Invention
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Macroencapsulation devices.
Macroencapsulation devices and related methods of manufacture are de... |
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Invention
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N-(hydroxyalkyl (hetero)aryl) tetrahydrofuran carboxamide analogs as modulators of sodium channel... |
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Invention
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Substituted tetrahydrofuran-2-carboxamides as modulators of sodium channels.
Compounds of formul... |
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Invention
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Hydroxy and (halo)alkoxy substituted tetrahydrofurans as modulators of sodium channels.
Compound... |
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Invention
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Solid dosage forms and dosing regimens comprising (2r,3s,4s,5r)-4-[[3-(3,4-difluoro-2-methoxy-phe... |
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Invention
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Stem cell differentiation and polymers.
Disclosed herein are compositions and methods related to... |
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2021
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Invention
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Enhanced differentiation of beta cells.
Provided herein are, inter alia, compositions and method... |
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Invention
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Modulators of cystic fibrosis transmembrane conductance regulator.
This disclosure provides modu... |
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Invention
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In vitro differentiation of pancreatic endocrine cells.
Disclosed herein are compositions and me... |
