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2025
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P/S
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Providing health information to patients and caregivers; providing health care information; provi... |
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P/S
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Providing medical information, namely, consumer product information regarding medical products to... |
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P/S
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Pharmaceuticals and medicines for the treatment of cystic fibrosis, pain, sickle cell disease, be... |
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P/S
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Providing health information to patients, caregivers and health care professionals; providing hea... |
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2024
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Invention
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Crystalline forms of c21h22cl2n4o2.
The present invention provides crystalline forms of a compou... |
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Invention
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Compounds for the treatment of kidney disease. The disclosure provides polycystin-1 (PC1) correct... |
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Invention
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Crispr-cas9 modified cd34+ human hematopoietic stem and progenitor cells and uses thereof.
Provi... |
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Invention
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Heteroaryl compounds for the treatment of pain. Compounds, and pharmaceutically acceptable salts ... |
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Invention
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Methods of preparing modulators of sodium channels and solid forms of the same for treating pain.... |
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Invention
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Methods of preparing compounds for treating pain and solid forms thereof. Processes for preparing... |
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Invention
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Compositions and methods for enhancing aav therapy and decreasing tropism of aav to the liver.
C... |
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P/S
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Pharmaceutical preparations for the treatment of cystic fibrosis. |
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P/S
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Pharmaceutical preparations for the treatment of cystic
fibrosis. |
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Invention
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Solid forms of modulators of cystic fibrosis transmembrane conductance regulator. Crystalline for... |
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Invention
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Modulators of cystic fibrosis transmembrane conductance regulator. This disclosure provides modul... |
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Invention
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Differentiation of pancreatic endocrine cells.
Disclosed herein are compositions and methods rel... |
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P/S
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Pharmaceutical preparations for the treatment of cystic fibrosis |
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Invention
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Process for preparing (2s,4s,4's,6s)-2-methyl-6-(1-methyl-1h-1,2,3-triazol-4-yl)-2',-(trieluorome... |
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Invention
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Complement factor i-related compositions and methods.
Provided herein are Complement Factor I (C... |
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Invention
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Precise excisions of portions of exon 44, 50, and 53 for treatment of duchenne muscular dystrophy... |
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Invention
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Precise excisions of portions of exons for treatment of duchenne muscular dystrophy.
Composition... |
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Invention
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Differentiation of pancreatic endocrine cells. Disclosed herein are compositions and methods rela... |
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Invention
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Cell therapy for diabetes.
Disclosed herein are methods of treating a subject having diabetes wi... |
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Invention
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Cell therapy for diabetes. Disclosed herein are methods of treating a subject having diabetes wit... |
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Invention
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Macroencapsulation device implantation and transport system and methods.
Macroencapsulation impl... |
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Invention
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Gcn2 inhibitors and uses thereof.
The present invention provides compounds, compositions thereof... |
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Invention
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Materials and methods for treatment of human genetic diseases including hemoglobinopathies.
The ... |
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Invention
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Urea-containing agonists of orexin receptor type 2. Disclosed are compounds, compositions, and me... |
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Invention
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Materials and methods for treatment of duchenne muscular dystrophy.
The present application prov... |
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Invention
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Complement factor-i formulations.
Provided herein are pharmaceutically acceptable formulations c... |
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Invention
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Inhibitors of apol1 and methods of using same.
The disclosure provides at least one entity chose... |
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Invention
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Affinity purification methods for adeno associated viruses (aavs). Provided herein are isolated p... |
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Invention
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Methods for directing lipid nanoparticles in vivo. Compositions and methods for enhancing payload... |
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Invention
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Compact proteins. Disclosed herein are compositions of compact proteins such as compact nucleobas... |
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Invention
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Stem cell derived pancreatic islet differentiation.
Disclosed herein are compositions and method... |
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Invention
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Pharmaceutical compositions for treating cystic fibrosis.
A pharmaceutical composition comprisin... |
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P/S
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Educational services, namely, providing classes, seminars, and workshops in the fields of medicat... |
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Invention
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Islet cell manufacturing compositions and methods of use.
Disclosed herein are compositions and ... |
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Invention
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Gene editing of regulatory elements.
Compositions and methods for disrupting and/or excising reg... |
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P/S
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Pharmaceuticals and medicines for the treatment of cystic
fibrosis, pain, sickle cell disease, b... |
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2023
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P/S
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Pharmaceuticals and medical treatment products in the field of diabetes; cell therapy products fo... |
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P/S
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Pharmaceuticals and medical treatments in the field of diabetes; cell therapy products for medica... |
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P/S
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Pharmaceuticals and medical treatments in the field of
diabetes; cell therapy products for medic... |
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P/S
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Pharmaceuticals and medical treatment products in the field
of diabetes; cell therapy products f... |
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P/S
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Pharmaceutical preparations for treating diabetes; medical treatments in the nature of anti-diabe... |
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P/S
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Pharmaceutical preparations for treating diabetes; medical
treatments in the nature of anti-diab... |
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Invention
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Substituted tetrahydrofurans as modulators of sodium channels. Compounds, and pharmaceutically ac... |
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Invention
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Crystalline forms of cftr modulators.
Crystalline forms of Compound I:
Crystalline forms of Co... |
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Invention
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Modulators of alpha-1 antitrypsin.
The disclosure provides compounds useful for treating alpha-1... |
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Invention
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Modulators of cystic fibrosis transmembrane conductance regulator, pharmaceutical compositions, m... |
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P/S
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medical and scientific research; medical and scientific research in the field of gene therapy; me... |
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Invention
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Cell housing device.
The present disclosure provides a cell housing device and a method of manuf... |
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P/S
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Providing on-line non-downloadable software for use by healthcare professionals to view and acces... |
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P/S
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Providing health information in the field of sickle cell disease; providing health care informati... |
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Invention
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4',5'-dihydrospiro[piperidine-4,7'-thieno[2,3-c]pyran] derivatives as inhibitors of apol1 and met... |
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Invention
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Modulators of cystic fibrosis transmembrane conductance regulator.
This disclosure provides modu... |
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2022
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Invention
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Stem cell differentiation and chemical compounds.
Disclosed herein are compositions and methods ... |
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Invention
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Macroencapsulation devices.
Macroencapsulation devices and related methods of manufacture are de... |
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Invention
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N-(hydroxyalkyl (hetero)aryl) tetrahydrofuran carboxamide analogs as modulators of sodium channel... |
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Invention
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Substituted tetrahydrofuran-2-carboxamides as modulators of sodium channels.
Compounds of formul... |
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Invention
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Hydroxy and (halo)alkoxy substituted tetrahydrofurans as modulators of sodium channels.
Compound... |
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Invention
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Stem cell differentiation and polymers.
Disclosed herein are compositions and methods related to... |
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2021
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Invention
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Enhanced differentiation of beta cells.
Provided herein are, inter alia, compositions and method... |
