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2025
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P/S
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Commercial promoting the interest of multiple sclerosis patients. Providing online chat rooms and... |
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P/S
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Pharmaceutical preparations for the treatment of hemophilia |
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Invention
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Methods for detecting aav.
Provided herein are methods for determining the serotype of a virus p... |
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Invention
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Methods for detecting aav. Provided herein are methods for determining the serotype of a virus pa... |
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2024
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Invention
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Biomarkers of methotrexate-induced immune tolerance.
The present application provides methods of... |
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Invention
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Image-based motor function assessment. Methods and systems are provided to assess physical moveme... |
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Invention
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Methods for treating cd20-related disorders. Disclosed are methods of treating various disorders ... |
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Invention
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Methods for treating digitally-identified cd20-related disorders.
Disclosed are methods of treat... |
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Invention
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Methods of treating neurodegenerative disorders. Provided herein are expression cassettes for exp... |
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Invention
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Methods of treating gaucher disease and gba-parkinson's disease. Provided herein are expression c... |
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Invention
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Methods of treating gaucher disease and gba-parkinson’s disease.
Provided herein are expression ... |
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Invention
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Methods of treating neurodegenerative disorders.
Provided herein are expression cassettes for ex... |
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Invention
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Human pah expression cassette for treatment of pku by liver-directed gene replacement therapy.
P... |
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Invention
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Modified-igg antibodies that bind transforming growth factor-beta1 with high affinity, avidity an... |
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Invention
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Systems and devices for producing biological products and methods of using the same.
Systems and... |
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Invention
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Predicting pharmacokinetic profiles of chemical compounds using machine learning. Methods, system... |
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P/S
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Downloadable software in the nature of a mobile application for enabling users to enter, access, ... |
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Invention
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Isoxazolidines as ripk1 inhibitors and use thereof.
The present disclosure relates to isoxazolid... |
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Invention
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Process for preparing shp2 inhibitors.
Provided herein are methods for preparing a SHP2 inhibito... |
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Invention
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Treatment of hemophilia a with fitusiran. The present disclosure provides methods for using fitus... |
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Invention
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Perfusion bioreactor with filtration systems.
The disclosure provides a filtration system for a ... |
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Invention
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Medicament delivery device. The present disclosure relates to a medicament delivery device compri... |
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Invention
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Medicament delivery device. A medicament delivery device comprises a housing, a needle, a needle ... |
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P/S
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Pharmaceutical preparations for the prevention and treatment of cardiovascular diseases and disea... |
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Invention
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Pyrazolyl compounds as emopamil binding protein inhibitors. Provided herein are compounds and pha... |
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Invention
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Integrated continuous manufacturing of therapeutic protein drug substances.
Provided herein are ... |
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Invention
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Bone-targeting antibodies.
Provided are recombinant and chemically-conjugated antibodies and fra... |
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Invention
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Analytical ultracentrifugation for characterization of recombinant viral particles.
Provided her... |
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Invention
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Methods of controlling the formation of disulfide bonds in protein solutions.
Disclosed herein a... |
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Invention
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Site-specific antibody-drug conjugation through glycoengineering.
The current disclosure provide... |
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Invention
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Glucosylceramide synthase inhibitors.
The invention relates to inhibitors of glucosylceramide sy... |
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Invention
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Treatment of cancer with anti-ilt2 antibodies.
The present invention relates to treatment of can... |
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Invention
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Treatment of cancer with anti-ilt2 antibodies. The present invention relates to treatment of canc... |
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Invention
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Substituted cyclic compounds and methods of treating phenylketonuria and other amino acidurias. T... |
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Invention
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Process for preparing 4-(3,3-difluoro-2,2-dimethyl-propanoyl)-3,5-dihydro-2h-pyrido[3,4-f][l,4]ox... |
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Invention
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Sleep-wake classification using machine learning. Methods, systems, and apparatus, including comp... |
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Invention
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Treatment of multiple sclerosis with anti-cd40l antibodies.
The present invention relates to tre... |
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Invention
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Treatment of multiple sclerosis with anti-cd40l antibodies. The present invention relates to trea... |
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Invention
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Fluid transfer device. A fluid transfer device for transferring a fluid between a diluent contain... |
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Invention
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Fluid transfer device. A fluid transfer device includes a body, a first connecting portion compri... |
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Invention
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Fluid transfer device. A fluid transfer device includes a body having a first connecting portion ... |
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Invention
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Marker for acid sphingomyelinase disorders and uses thereof.
The present disclosure provides met... |
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Invention
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Humanized anti-complement factor bb antibodies and uses thereof.
Provided herein are humanized a... |
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Invention
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Multi-vial adapters for reconstituting or diluting lyophilized or concentrated drug products. The... |
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Invention
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Collar hold detent mechanism and lock for injection devices. This application relates to an injec... |
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Invention
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Rotatable collar for injection devices. An injection device comprising: an injection device body;... |
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Invention
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Hold detent mechanism for injection devices. Some injection devices include an injection device b... |
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Invention
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Needle shroud latch for injection devices. An injection device includes a housing, a needle shrou... |
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Invention
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Treatment of dry age-related macular degeneration.
The present disclosure provides gene therapy ... |
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Invention
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Injector device. A medicament delivery device for reducing a force required to activate the devic... |
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Invention
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Medicament delivery device. A medicament delivery device includes a needle disposed at a distal e... |
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Invention
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Injector device. A medicament delivery device reduces a force required for activation, and the me... |
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2023
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P/S
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Pharmaceutical products for the prevention and treatment of immunological diseases; pharmaceutica... |
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P/S
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Pharmaceutical products for the prevention and treatment of immunological diseases, pharmaceutica... |
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P/S
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Pharmaceuticals for use in the treatment of lysosomal storage diseases |
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P/S
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Support services for patients and caregivers in the field of rare genetic diseases and disorders,... |
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P/S
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Pharmaceutical preparations for the treatment of autosomal dominant polycystic kidney disease; ph... |
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2022
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Invention
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Fitusiran for use in improving patient-reported outcome in hemophilia patients.
The present disc... |
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P/S
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Pharmaceutical preparations for the treatment of hemophilia. Downloadable mobile application in t... |
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P/S
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Pharmaceutical preparations for the treatment of rare diseases notably lysosomal storage disorders. |
